The phase 3 STEER study enrolled 127 treatment-naïve patients aged 2 to less than 18 years with SMA type 2 who were able to sit but had never walked independently.

Between 1999 and 2022, there were 63,550,429 deaths in the US, of which 0.06% had cold recorded as an underlying or contributing cause of death. (HealthDay News) — From 1999 to 2022, there was ...

Compared with 2022, in 2023, state and local governments accounted for a higher share of spending. (HealthDay News) — Health care spending in the United States reached $4.9 trillion and ...

(HealthDay News) — For adults with migraine, atogepant 60mg once daily was superior to placebo for efficacy and functional measures of treatment across 3 trials, according to research published online ...

The approval was based on data from the randomized, placebo-controlled, double-blind, phase 3 RATIONALE-305 trial.

According to Vertex Pharmaceuticals, approximately 300 additional people with CF are now eligible to receive treatment.