Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...

For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...

Gene therapy is linked to better nonmotor outcomes in spinal muscular atrophy type 1 compared to first-line nusinersen, new ...

A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...

New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...

The goal of gene therapy is to permanently cure hereditary diseases. One of the most promising technologies for this is the ...

This sponsored article was provided by a partner and is not editorial content from Los Angeles Magazine or the Engine Vision Media Network. Every cell in your body holds a unique genetic code within ...

University of Bristol researchers have discovered a VEGF-C gene therapy that protects the kidneys in people with type 1 ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

A new 3D human brain tissue platform developed by MIT researchers is the first to integrate all major brain cell types, ...

In a preclinical mouse study, gene therapy delivering VEGFC to kidney cells reduced early signs of kidney damage in Type 1 ...