The FDA last October paused Intellia Therapeutics’ late-stage CRISPR studies after detecting life-threatening enzyme ...
Clinical-stage biotechnology company Jaguar Gene Therapy has completed dosing in Cohort I of its first-in-human clinical ...
A study of 470,000 people reveals that the APOE gene could be behind 90% of Alzheimer's cases in the world today.
Gene therapies have the potential to cure some diseases, but they are extraordinarily expensive. Location can also be a big ...
In Partnership with ATC Genomics, the Company Presented One of Asia's Largest Real-World Datasets (n=12,281) for AI-Powered ...
An estimated 170,000 Australians were diagnosed with cancer in 2025. Many people know the causes of cancer are partly genetic. But how do your genes, which contribute so much of what makes you you, ...
Shares of uniQure plummeted more than 40% in premarket trading Monday after the company confirmed the FDA has rejected its current data package for AMT-130, a highly anticipated gene therapy for ...
Days after FDA Commissioner Marty Makary appeared to malign uniQure’s AMT-130 in an interview with CNBC, the agency confirmed ...
A Frisco mom’s yearslong fight led to a gene therapy breakthrough for the rare SLC6A1 disorder. Her son Maxwell is the first patient treated and is already showing promising progress.
Antisense oligonucleotides (ASOs), used to treat genetic diseases, can affect how cells repair damage to their DNA. This is ...
CRISPR gene drives bias inheritance in pests, advancing population-level control while raising questions about resistance and ...
Gene therapy has been successfully used to treat a number of diseases, including immune deficiencies, hereditary blindness, ...
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